Ep. 45: Breakthroughs in Sickle Cell Disease

Well Beyond Medicine: The Nemours Children's Health Podcast - Un pódcast de Nemours Children's Health - Lunes

You've probably heard the news: an FDA-approved treatment for sickle cell disease applying the gene-editing tool CRISPR is now available in the U.S. It's a landmark moment in medical science on two fronts: the treatment - called Casgevey - is the first FDA-approved regimen to utilize CRISPR technology to treat any genetic disease. And it's a huge leap forward in the treatment of sickle cell, a genetic disease affecting about 100,000 people in the U.S. - mostly African Americans. Today, we'll ...

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