548 Episodo

  1. Treating Huntington's Disease by Addressing Neuroinflammation

    Publicado: 24/6/2020
  2. How Patient Advocate-Led Research Can Alter a Rare Disease Landscape

    Publicado: 17/6/2020
  3. Keeping Clinical Trials Going During a Pandemic

    Publicado: 10/6/2020
  4. Looking for Commonalities in Rare

    Publicado: 3/6/2020
  5. Learning to Be Comfortable Being Uncomfortable

    Publicado: 27/5/2020
  6. An Approach to De-Risk Rare Disease Drug Development

    Publicado: 20/5/2020
  7. Targeting Epigenetics in Rare Proliferative Bone Marrow Cancers

    Publicado: 13/5/2020
  8. Chiesi Charges Ahead in Rare Disease

    Publicado: 6/5/2020
  9. Targeting the Metabolism of Rare Cancers

    Publicado: 29/4/2020
  10. Unlocking Bryson's Brain

    Publicado: 22/4/2020
  11. Living Therapies for Chronic Conditions

    Publicado: 15/4/2020
  12. A One-to-Many Approach to Gene Therapy for Retinal Disease

    Publicado: 8/4/2020
  13. Targeting an Immune Switch in Rare Diseases

    Publicado: 1/4/2020
  14. Targeting the Regulatory Genome to Treat Rare Blood Diseases

    Publicado: 25/3/2020
  15. A Reborn Forma Therapeutics Focuses on Rare Blood Diseases and Cancer

    Publicado: 18/3/2020
  16. Targeting Genetic Diseases at Their Root Cause

    Publicado: 11/3/2020
  17. Targeting Hormone Dysregulation in Prader-Willi Syndrome

    Publicado: 4/3/2020
  18. Rare Disease Advocates Take to the Hill

    Publicado: 25/2/2020
  19. Targeting a Common Link in Otherwise Different Rare Diseases

    Publicado: 19/2/2020
  20. Bringing Clinical Trials to Patients

    Publicado: 12/2/2020

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RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.

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