RARECast
Un pódcast de RARECast - Jueves
548 Episodo
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A Heart Attack that Led to a Rare Disease Diagnosis
Publicado: 30/1/2025 -
Targeting Rare Liver Diseases with Gene Editing Therapies
Publicado: 23/1/2025 -
Using AI to De-Risk Rare Disease Drug Development
Publicado: 16/1/2025 -
Addressing a Growing Demand for Plasma-Derived Therapies
Publicado: 9/1/2025 -
Empowering Patients with Data to Drive Drug Development
Publicado: 2/1/2025 -
How Advocates Are Advancing a Treatment for an Ultra-Rare Disease
Publicado: 26/12/2024 -
Engineering B Cells to Produce Therapeutic Proteins
Publicado: 19/12/2024 -
A Pipeline Win as BridgeBio Learns to Balance Theory with Practice
Publicado: 12/12/2024 -
Considering What It Will Take for Payers to Embrace Advances in Sequencing
Publicado: 5/12/2024 -
Finding Strength
Publicado: 27/11/2024 -
A Non-Profit Works to Advance a DMD Gene Therapy
Publicado: 21/11/2024 -
Accepting What We Can’t Understand
Publicado: 14/11/2024 -
A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter
Publicado: 7/11/2024 -
Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection
Publicado: 31/10/2024 -
Scaling N-of-1 Therapies to Viability
Publicado: 24/10/2024 -
Building Gene Therapies that Address Gain and Loss of Function Simultaneously
Publicado: 17/10/2024 -
How One Woman Climbed from Patient to Advocate
Publicado: 10/10/2024 -
Shortening the Diagnostic Odyssey
Publicado: 3/10/2024 -
Making Exomes More Revealing
Publicado: 26/9/2024 -
How One Patient Organization Catalyzed Drug Development
Publicado: 19/9/2024
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
